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Gene Therapy & Genomic Medicine
CRISPR edits, delivery vectors, rare‑disease trials, and approvals.
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Latest in Gene Therapy & Genomic Medicine
News: Clinical-Scale WAS Editing Meets GMP and Safety Benchmarks
7+ hour, 19+ min ago (367+ words) Clinical-Scale WAS Editing Meets GMP and Safety Benchmarks CRISPR Medicine News Clinical-Scale WAS Editing Meets GMP and Safety Benchmarks A UCL-led team has developed a clinical-scale CRISPR-Cas9-AAV6 workflow intended to correct Wiskott-Aldrich syndrome in haematopoietic stem and progenitor cells, reaching…...
xBxBio Completes Internal Review of Regulatory Framework Ahead of Final Release
8+ hour, 24+ min ago (58+ words) openPR.com xBxBio Completes Internal Review of Regulatory Framework Ahead of Final Release Press release from: xBxBio xBxBio - Advancing Connected Cardiovascular Intelligence Permanent link to this press release: You can edit or delete your press release xBxBio Completes Internal Review…...
Researchers Uncover ‘Pervasive’ Artifact Inflating Gene Knockdown Measures
19+ hour, 37+ min ago (18+ words) GenomeWeb Researchers Uncover âPervasiveâ Artifact Inflating Gene Knockdown Measures...
She Can’t Feel Pain or Anxiety. Her Genetic Mutations Hold the Key to Eliminating Human Suffering, Scientists Claim.
13+ hour, 22+ min ago (344+ words) A life without pain seems miraculous. But denying this hallmark of human existence could come with its own set of challenges. Cameron was diagnosed with “pain insensitivity disorder,” which covers a spectrum of conditions that spring from a well of…...
Skeletal editing can transform molecules’ biological activity
20+ hour, 21+ min ago (238+ words) Federation: Log in through a federation service that connects your organization to multiple systems. Use this option if your organization instructs you to use federated sign-in. Oxygen-to-nitrogen swap changes a natural product’s mechanism of action Researchers in Korea have used…...
Custom genetic codes can now be created with ease
21+ hour, 5+ min ago (425+ words) Federation: Log in through a federation service that connects your organization to multiple systems. Use this option if your organization instructs you to use federated sign-in. Custom genetic codes can now be created with ease Nearly every organism on the…...
SANA: IND and phase I/II trial for diabetes therapy and first-in-human CAR T data expected within 12 months
22+ hour, 32+ min ago (94+ words) TradingView SANA: IND and phase I/II trial for diabetes therapy and first-in-human CAR T data expected within 12 months Two innovative platforms are advancing: a hypoimmune cell therapy for type 1 diabetes, with an IND and phase I/II trial planned…...
CRISPR-Combo Speeds Gene-Edited Crop Regeneration
1+ day, 1+ hour ago (506+ words) Editing a plant’s genes is only one step in developing an improved crop. Scientists must also regenerate a complete plant from a small number of edited cells — a process that can be slow, unreliable or impossible in some species. Researchers…...
Cracking cell dynamics with single-cell proteomics and CRISPR
5+ day, 1+ hour ago (425+ words) Sponsored by Cell Signaling Technology and Myllia Join this virtual panel to explore how combining pooled CRISPR screening with intracellular protein detection can reveal cellular responses and signalling dynamics that transcriptomics alone may miss. Single-cell transcriptomics can show which genes…...
Cellectis scraps CAR-T pipeline in gene editing pivot - European Biotechnology Magazine
1+ day, 7+ hour ago (424+ words) French biotech Cellectis is abandoning development of its two internal allogeneic CAR-T programs and repositioning itself as an in vivo gene editing company focused initially on cardiovascular disease. Why it matters: The move is a dramatic reset for one of…...